Congenital dyserythropoietic anemia type IV explained

Congenital dyserythropoietic anemia type IV (CDA IV) has been described with typical morphologic features of CDA II but a negative acidified-serum test.[1]

Presentation

CDA type IV is characterized by mild to moderate splenomegaly. Hemoglobin is very low and patients are transfusion dependent. MCV is normal or mildly elevated. Erythropoiesis is normoblastic or mildly to moderately megaloblastic. Nonspecific erythroblast dysplasia is present.[2]

Genetics

Congenital dyserythropoietic anemia type IV is an autosomal dominant inherited red blood cell disorder characterized by ineffective erythropoiesis and hemolysis resulting in anemia. Circulating erythroblasts and erythroblasts in the bone marrow show various morphologic abnormalities. Affected individuals with CDAN4 also have increased levels of fetal hemoglobin.[3]

Treatment

Treatment consists of frequent blood transfusions and chelation therapy. Potential cures include bone marrow transplantation and gene therapy.

See also

Further reading

Notes and References

  1. Web site: Congenital dyserythropoietic anemia type II: Epidemiology, clinical appearance, and prognosis based on long-term observation . 2011-09-26 . dead . https://archive.today/20120709115538/http://bloodjournal.hematologylibrary.org/content/102/13/4576.full.html . 2012-07-09 .
  2. Book: Manual of Pediatric Hematology and Oncology - Google Books . 2005-06-06 . 2015-05-06 . 9780123751553 . Lanzkowsky . Philip . Academic Press . https://web.archive.org/web/20191217040334/https://books.google.com/books?id=f5C246w1ec4C . 2019-12-17 . dead .
  3. Web site: ANEMIA, CONGENITAL DYSERYTHROPOIETIC, TYPE IV; CDAN4. Omim.org. 6 May 2015.